- New articles: Cell
Prime editing and base editing in mouse models and human cells effectively correct mutations in a gene that causes a childhood neurodevelopmental disorder called alternating hemiplegia of childhood In vivo prime editing in the brain results in significant improvements in neurological symptoms and lifespan, highlighting a potential one-time gene therapy approach for the disorder
- Cell | Journal | ScienceDirect. com by Elsevier
Cell publishes findings of unusual significance in any area of experimental biology, including but not limited to cell biology, molecular biology, neuroscience, immunology, virology and microbiology, cancer, human genetics, systems biology, signaling, and disease mechanisms and therapeutics The basic criterion for considering papers is whether the results provide significant conceptual
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